Gene Therapy Initiative 1st Annual Symposium - No CME

Don’t miss this opportunity at the Gene Therapy Initiative 1st Annual Symposium on September 19, 2024 to engage our thriving San Diego community of researchers, life sciences, biotechnology and pharmaceutical companies in the gene therapy space.

Objective:
The Gene Therapy Initiative (GTI) Symposium will convene researchers and industry experts to share the latest scientific findings and facilitate new partnerships with the goal of expediting the delivery of stem cell and gene therapy treatments, especially for patients with rare genetic diseases.

Program Highlights:

• Exploratory talks on innovative gene modifying therapeutics and optimization of existing tools.
• Updates on gene therapies that are the subject of academic research and commercial development.
• Induced Pluripotent Stem-cell-based disease models to test gene therapies.
• Interactive panel on resources and collaboration for developing therapies for rare diseases.
• Opportunity to learn about 2024 GTI seed grant funded projects.
• Poster session featuring faculty and student research.
• Networking hour to foster connectivity amongst attendees.

Featured Sessions and Speakers: For full program, visit our symposium website: https://genetherapy.ucsd.edu/symposium-2024/

Session 1: Ex Vivo Gene Therapy

• Masayuki Kai, PhD, Vice President and Head of Research, Kyowa Kirin, Inc.
  *Keynote Speaker
• Stephanie Cherqui, PhD, Director of the Gene Therapy Initiative, Professor, Department of Pediatrics, UC San Diego
  

Session 2: AAV Gene Therapy

• Farah Sheikh, PhD, Professor, Department of Medicine, UC San Diego
• Brian Head, PhD, Professor, Department of Anesthesiology, UC San Diego
• Loren Looger, PhD, Professor, Department of Neurosciences, UC San Diego
• Nayla Mumneh, MD, Executive Medical Director, NeuroMuscular, Novartis Pharmaceuticals Corporation

Session 3: Testing Gene Therapies in Induced Pluripotent Stem Cell Models

• Alysson Muotri, PhD, Co-Director of the Gene Therapy Initiative Professor, Department of Pediatrics, UC San Diego
• Angels Almenar-Queralt, PhD, Assistant Professor, Pediatrics

Session 4: Resources & Collaborations for Gene Therapy Development

• Rodica Stan, PhD, Senior Scientific Project Manager, Therapeutic Development Branch, National Center for Advancing Translational Sciences, National Institutes of Health, Platform Vector Gene Therapy [PaVe-GT]
• Nancy Stack, Patient Advocate
• CIRM

Session 5: RNA Technologies

• Nicole Coufal, MD, PhD, Associate Professor, Pediatrics, UC San Diego
• Gene Yeo, PhD, MBA, Professor, Cell and Molecular Medicine, UC San Diego
• Holly Kordasiewicz, PhD, Vice President Neurology Research, Ionis Pharmaceuticals, Inc.

There is No CME for this activity.

Registration Fees

Online Registration is now closed. Contact [email protected] if you have any questions.

Cancellation Policy
The full course tuition is refundable, less $25 if your cancellation is received in writing, on or before September 9, 2024. No refunds will be allowed after this date. In the unlikely event that the course is canceled, UC San Diego is responsible only for a full refund of the registration fee.

  Sanford Consortium
  Duane Roth Auditorium
  2880 Torrey Pines Scenic Dr.
  La Jolla, CA 92037
  DIRECTIONS

 
Parking: 

Spaces have been reserved for this event in the Sanford Consortium Parking Lot P385 marked with the event title. Spaces are limited and first come/first serve. 
If you do not find a space in this lot, there are other options available:

• Closest Parking Lot – Torrey Pines Center South (North Torrey Pines Road, at the end of North Point Drive)
• Closest Parking Lot – Torrey Pines Center North (North Torrey Pines Road, across from campus)
• Glider Port Dirt Lot #P386 - Full day parking is $3.25

Mitigation of Relevant Financial Relationships

The UC San Diego School of Medicine adheres to the ACCME Standards for Integrity and Independence in Accredited Continuing Education. 

Contact Us

Registration Questions
UC San Diego School of Medicine
Continuing Professional Development 
9500 Gilman Drive, MC0947
La Jolla, CA 92093-0947
P: (858) 534-3940 / Toll-Free: (888) 229-6263
F: (858) 534-1896
E-mail: [email protected]
Website: cpd.ucsd.edu

Conference Planner
Amy Hart
Program Manager, Education & Collaboration
Phone: (858) 822-4770
E-mail: [email protected]

Thank you to the following companies for supporting this symposium.

California Institute for Regenerative Medicine (CIRM)

Thermo Fisher Scientific

Lexeo Therapeutics

Mahzi Therapeutics

Papillon Therapeutics

Kyowa Kirin

MaxCyte

UC San Diego Sanford Stem Cell Clinical Center

Avid Bioscience

Additional Sponsorship and Exhibitor Opportunities Available

Contact [email protected] for more information on sponsoring. 

Sponsorship Info Sheet

For more information, visit our symposium website: https://genetherapy.ucsd.edu/symposium-2024